A groundbreaking study has shed light on the complex interactions between dystrophin, a protein critical to muscle stability, and its partner protein, dystrobrevin, offering new pathways for understanding and treating Duchenne Muscular Dystrophy (DMD).
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- Our short film, ‘Lov-Able,’ heads to Australian disability-led film festival
- PPMD Honored with RAPS 2026 Patient-Centered Health Award
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- FDA set to decide on experimental DMD treatment in early 2027
- FDA Accepts Dyne Therapeutics’ Biologics License Application for Z-Rostudirsen
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