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Finding harmony and inclusion in life through music
Living with Duchenne muscular dystrophy (DMD) has taught me countless lessons, especially the power of […]
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CureDuchenne’s latest investment aims to address the limitations of current AAV-delivered gene therapy treatments for Duchenne muscular dystrophy (DMD).
Our recent investment in Entos Pharmaceuticals (https://entospharma.com) aims to explore the potential of their non-viral, […]
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Elevidys halted in nonambulatory DMD after second death reported
A second person with Duchenne muscular dystrophy (DMD) has died of acute liver failure after […]
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Insights by Ira: Let’s Get Active This Summer!
It’s the most wonderful time of the year! The holiday’s season already? No! Summertime! That’s […]
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A Safety Update on ELEVIDYS – June 2025
We are heartbroken to learn of the loss of another member of our community following […]
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Sarepta pauses Duchenne gene therapy for non-ambulatory individuals after second death due to acute liver failure
CureDuchenne is sad to share that another person has passed away due to acute liver […]
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MDA Ambassador Guest Blog: How Making an Impact Renewed My Purpose After FSHD Diagnosis
Ranae Beeker, who is in her late 60s, has found her greatest joy in her […]
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REGENXBIO WEBINAR
AFFINITY DUCHENNE®: New Phase 1/2 Interim Functional Data Watch HERE The post REGENXBIO WEBINAR appeared […]
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Our family’s all-star football player also lives with Duchenne
I’m a mother of seven and a caregiver to the three of my sons who […]
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PPMD Announces Children’s Hospital of Philadelphia as CDCC, Recipient of Inaugural Clinical Research Designation
PPMD is pleased to announce the expansion of its renowned Certified Duchenne Care Center (CDCC) […]
