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What’s it like to have three sons living with DMD?
What’s it like to have three children with Duchenne muscular dystrophy (DMD)? That’s the question […]
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I tried home health physical therapy, but will I keep exercising?
In a column I wrote last month, I talked about finally deciding to try some […]
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Engineered tRNA fixes faulty dystrophin protein in DMD mice
An engineered transfer RNA (tRNA) molecule developed by hC Bioscience could be a fix for […]
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Viltepso fails main goal in confirmatory Phase 3 study
After nearly a year of treatment, Viltepso (viltolarsen) was well tolerated and tended to increase […]
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What I take away from watching the filmed version of ‘Hamilton’
Last week, my girlfriend and I caught the 2020 filmed version of Lin-Manuel Miranda’s award-winning […]
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NS Pharma Shares Update on VILTEPSO® (Viltolarsen) Phase 3 Study
NS Pharma, Inc. has shared preliminary analysis results from RACER53, the global Phase 3 clinical […]
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Meeting of the Minds 2024
As we prepare to welcome families to the CureDuchenne FUTURES Annual Conference, scientific leaders, executives […]
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Our son’s graduation from high school was beautifully exhausting
My oldest son, Max, 18, graduated from high school last Sunday. Graduation is a milestone […]
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hC Bioscience Announces Program in Duchenne Muscular Dystrophy and Reports In Vivo Data From tRNA-based Protein Editing Platform
As a funder of hC Bioscience, we’re happy to have them announcing their tRNA-based approach […]
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Awareness Initiatives and Innovative Therapeutic Approaches Bring Hope to People Living with Becker Muscular Dystrophy
The following content is sponsored by Edgewise Therapeutics and does not reflect the views of […]