Muscular Dystrophy News — ScienceDaily Medical research on muscular dystrophy and myopathy. Read about the promise of stem cell research for muscular dystrophy patients, and successful treatments tested in dogs.
- New study uncovers key insights into protein interactions in Duchenne muscular dystrophy, paving way for more targeted therapieson December 31, 2024 at 6:41 pm
A groundbreaking study has shed light on the complex interactions between dystrophin, a protein critical to muscle stability, and its partner protein, dystrobrevin, offering new pathways for understanding and treating Duchenne Muscular Dystrophy (DMD).
- New drug shows promise against Duchenne muscular dystrophyon December 16, 2024 at 5:56 pm
A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. Researchers have discovered that an experimental compound called K884 can boost the natural repair abilities of muscle stem cells. Current treatments can slow muscle damage, but don’t address the root problem.
- New discovery enables gene therapy for muscular dystrophies, other disorderson November 14, 2024 at 9:11 pm
StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.
- Mouse model reveals liver involvement in muscular dystrophyon October 24, 2024 at 6:55 pm
A new mouse model mimicking the liver symptoms of myotonic dystrophy type 1 — the most prevalent form of adult-onset muscular dystrophy — provides insight into why patients develop fatty liver disease and display hypersensitivity to medications, making treatment difficult. The new model opens avenues for screening new medications for liver toxicity prior to patient trials.
- New gene therapy approach shows promise for Duchenne muscular dystrophyon July 24, 2024 at 11:12 pm
Researchers have made a significant breakthrough in developing a new gene therapy approach that restores full-length dystrophin protein, which could lead to new treatments for people with Duchenne muscular dystrophy (DMD).