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How I’ve gotten through a busy season in the life of my family
My life has recently been a whirlwind of activity. Now that the dust is finally […]
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Marking ’30 Days of Strength’ for MD Awareness Month this year
The muscular dystrophy (MD) community is poised to mark National Muscular Dystrophy Awareness Month with […]
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RAG-18 granted FDA orphan drug status for Duchenne, Becker MD
The U.S. Food and Drug Administration (FDA) has granted orphan drug status to RAG-18, being […]
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Making memories on what was likely my last family vacation
My wife, Wendy, and I recently enjoyed a beach vacation in North Carolina with our […]
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Elevidys, one year later: ‘It’s no longer just about coping with DMD’
A little over a year ago, neurologist Sarah Wright administered Elevidys (delandistrogene moxeparvovec-rokl) to then […]
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Living on campus is new territory for one son with DMD
My past two columns highlighted significant life events: my daughter’s wedding and my return to […]
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Duchenne Added to Massachusetts Newborn Screening Panel
PPMD is excited to announce another significant milestone: Massachusetts has officially approved the addition of […]
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Champions in Dallas: An Evening of Culinary Delight and Philanthropy to Support CureDuchenne
Dallas’ Finest Will Unite to Advance Innovative Research and Care for Duchenne Muscular Dystrophy Dallas, […]
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FDA gives WVE-N531, exon 53 skipping therapy, supportive status
The U.S. Food and Drug Administration (FDA) has given WVE-N531, an investigational therapy for Duchenne […]
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For Duchenne survivors, dealing with grief provides us strength
Earlier this month, I attended the debut of Stephanie Esther Fam’s play “Absence” at Singapore’s […]
