Kids News

Satellos Bioscience Inc. has announced encouraging data from the company’s Phase 1b open-label study of SAT-3247, an oral small molecule inhibitor of AAK, designed to address progressive muscle loss by restoring muscle regeneration in response… The post Satellos Announces Positive Functional Data from Phase 1b Open-Label Trial of SAT-3247 in Adults with Duchenne appeared first on Parent Project Muscular Dystrophy.

We are delighted to share exciting news for the Duchenne community: Governor Ron DeSantis has officially signed Florida’s Duchenne newborn screening legislation (HB 1089 / SB 524) into law. With this historic act, Florida becomes… The post Florida Signs Duchenne Newborn Screening into Law appeared first on Parent Project Muscular Dystrophy.

PPMD is closely monitoring the U.S. House of Representatives Energy and Commerce Committee markup of the Committee’s budget reconciliation text, scheduled for tomorrow, Tuesday, May 13, 2025, at 2:00 PM ET. Updated legislative language released… The post Budget Reconciliation Update and the Impact on Medicaid appeared first on Parent Project Muscular Dystrophy.

Ten years ago, the Duchenne community gained a vital tool for the clinical management of adrenal insufficiency and steroid stress dosing for individuals on long-term corticosteroid therapies: the PJ Nicholoff Steroid Protocol for Healthcare Providers…. The post A Decade of Impact: Honoring PJ’s Protocol and Its Legacy appeared first on Parent Project Muscular Dystrophy.

On April 3, 2025, the U.S. Department of Health and Human Services (HHS) announced the dissolution of the Advisory Committee on Heritable Disorders in Newborns and Children (ACHDNC), an unexpected development that has left a… The post An Update on PPMD’s Continued Strategy for Advancing Duchenne Newborn Screening appeared first on Parent Project Muscular Dystrophy.