- Cumberland Pharmaceuticals Announces Positive Results from Phase 2 FIGHT DMD Trial of Ifetroban for Treatment of Duchenne Cardiomyopathyby Parent Project Muscular Dystrophy on February 4, 2025 at 5:56 pm
Cumberland Pharmaceuticals Inc. has announced positive top-line results from its Phase 2 FIGHT DMD trial evaluating ifetroban for the treatment of Duchenne cardiomyopathy. Ifetroban is an oral thromboxane receptor antagonist aimed at reducing inflammation and… The post Cumberland Pharmaceuticals Announces Positive Results from Phase 2 FIGHT DMD Trial of Ifetroban for Treatment of Duchenne Cardiomyopathy appeared first on Parent Project Muscular Dystrophy.
- Sarepta Therapeutics Announces Results from Part 2 of EMBARK Study of ELEVIDYSby Parent Project Muscular Dystrophy on January 27, 2025 at 7:14 pm
Sarepta Therapeutics, Inc. has announced positive topline results from Part 2 of EMBARK, the company’s Phase 3 clinical study of ELEVIDYS. ELEVIDYS is a micro-dystrophin gene therapy used for the treatment of individuals aged four… The post Sarepta Therapeutics Announces Results from Part 2 of EMBARK Study of ELEVIDYS appeared first on Parent Project Muscular Dystrophy.
- Update from PPMD’s 2025 Duchenne Healthcare Professionals Summitby Parent Project Muscular Dystrophy on January 23, 2025 at 5:22 pm
PPMD recently convened over 360 healthcare professionals, researchers, and industry partners, including representatives from the FDA, NIH, CDC, and international representatives in one room to discuss the latest updates in dystrophinopathy care and research at… The post Update from PPMD’s 2025 Duchenne Healthcare Professionals Summit appeared first on Parent Project Muscular Dystrophy.
- Race to End Duchenne Kicks Off 20th Anniversary at Walt Disney World Marathon Weekendby Parent Project Muscular Dystrophy on January 17, 2025 at 7:07 pm
The Race to End Duchenne program is celebrating our 20th anniversary in 2025, and we spent the weekend of January 8-12 kicking it off at the place where it all began – the Walt Disney… The post Race to End Duchenne Kicks Off 20th Anniversary at Walt Disney World Marathon Weekend appeared first on Parent Project Muscular Dystrophy.
- PPMD Advocacy in the 119th Congress and the 47th Administrationby Parent Project Muscular Dystrophy on January 16, 2025 at 2:37 pm
As the 119th Congress and the 47th Administration prepare to take office, PPMD is committed to furthering the needs of our community through comprehensive, creative, and tenacious advocacy on Capitol Hill, regardless of politics. Over… The post PPMD Advocacy in the 119th Congress and the 47th Administration appeared first on Parent Project Muscular Dystrophy.