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Setting Up A Successful School Year
Setting Up A Successful School Year PPMD is here to make sure that families within […]
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PPMD Community Webinar Recap: Overview of DUVYZAT and Access Resources
On September 18, 2024, PPMD hosted an informative community webinar featuring representatives from ITF Therapeutics, […]
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Overcoming mental hurdles as I transition to using a walker
I’ve had a walker with wheels for a decade. I got it after back surgery […]
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PPMD & Global Patient Advocacy Groups Award BIND Project $113,000 to Further Brain Involvement Research
PPMD is thrilled to announce that we have collaborated with a number of patient organizations […]
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Why patient advocacy is important for those of us with Duchenne
Last Saturday, I had the honor of participating in the third Singapore Health Patient Advocate […]
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Losmapimod fails to significantly improve FSHD outcomes: Study
Losmapimod, an investigational medication from Fulcrum Therapeutics, failed to significantly outperform a placebo at improving […]
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Navigating Access & Resources
Navigating Access & Resources Navigating insurance access for medical care such as approved therapies or […]
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A friend in the DMD world makes a difference in my self-care
In my recent columns, I’ve shared several challenges we’ve faced in the past months of […]
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NS Pharma DMD treatment gets FDA rare pediatric disease status
The U.S. Food and Drug Administration has granted rare pediatric disease designation to NS-050/NCNP-03, an […]
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Atamyo, Dion Foundation partner to expand LGMD study into US
Atamyo Therapeutics has partnered with the Dion Foundation for Children with Rare Diseases to expand […]
