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A walker should help prevent falls, right?
I’m getting more comfortable using my walker. However, it just doesn’t pay to trust the
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Equitable Access in Clinical Trials—A Call for Action and Collaboration
Living with Duchenne and Becker presents unique challenges, especially for families from underserved or marginalized
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DMD gene therapy GNT0004 set to enter Phase 3 trial in Europe, US
GNT0004, an experimental gene therapy for Duchenne muscular dystrophy (DMD), appears to be working as
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Taking control when living with limb-girdle muscular dystrophy
The power to influence or even direct people’s behavior or the course of events is
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Changes this year helped me learn my limitations as a caregiver
Life feels busy, which is no surprise to me. My husband, Jason, and I share
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Regenxbio starts pivotal trial testing DMD gene therapy RGX-202
Regenxbio has initiated the pivotal phase of a clinical trial testing its experimental gene therapy
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How I experienced inclusion (and didn’t) during my education
On Saturday, I presented at the Participation — Inclusion in Action Conference 2024, which was
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WATCH: RGX-202 – AFFINITY DUCHENNE Pivotal Program and Functional Data (Webinar Recording)
REGENXBIO recently joined PPMD for a community webinar to provide an update on its AFFINITY
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PPMD Culminates 30th Anniversary with Celebratory “Investing in Every Future” Event
PPMD commemorated its 30th anniversary with the “Investing in Every Future” celebratory event on November
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New technology may inform effective MD gene therapies: Study
A new technology called StitchR effectively restored the production of large muscle proteins dystrophin and
