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Solid Biosciences Shares Initial Data from INSPIRE DUCHENNE Study of Gene Therapy Candidate SGT-003
Solid Biosciences Inc. has announced positive initial data from the company’s Phase 1/2 INSPIRE DUCHENNE
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MD trial update: 5 OPMD patients safely treated with gene therapy
Five people with oculopharyngeal muscular dystrophy (OPMD) — a type of muscular dystrophy marked by
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A week in the life of an overwhelmed caregiver
I’ll be straightforward about caregiving: It’s exhausting. I’m the mother of seven children: Lexi, 23,
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Phase 1 trial of SAT-3247 finishes enrolling healthy volunteers
A Phase 1 clinical trial testing SAT-3247, an oral treatment candidate for Duchenne muscular dystrophy
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It started with shoes, but now everything is too heavy
One thing I was born with, aside from my facioscapulohumeral muscular dystrophy (FSHD), was narrow
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World of Warcraft event raises $2M to support DMD research, care
A fundraiser through the online role-playing game World of Warcraft has raised more than $2
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Growing into limb-girdle muscular dystrophy — and, better, marriage
I’ve been married for 11 years. Before then, as I grew up with what I
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Blizzard Entertainment® Raises Over $2 Million for CureDuchenne Through World of Warcraft ® Charity Pet Program, Funding Lifesaving Duchenne Muscular Dystrophy Research
Inspired by “The Remarkable Life of Ibelin” documentary, Players Around the World Uniteto Honor Mats
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Napa in Newport Returns for Its 11th Annual Celebration of Wine, Culinary Excellence, and Philanthropy
Southern California’s Premier Wine Gala Set for March 1, 2025, at Pendry Newport Beach NEWPORT
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Phase 2 trial shows DMD treatment ifetroban boosts heart function
Treatment with oral therapy ifetroban led to improvements in measures of heart function in people
