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This time, new medical equipment is hard for me to accept
Our house is getting a new piece of medical equipment this week. That’s happened before, […]
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Rare pediatric disease designation granted to LAMA2-CMD therapy
The U.S. Food and Drug Administration (FDA) has granted rare pediatric disease designation to MDL-101, […]
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WATCH: Interim Results from FORWARD-53 Study of WVE-N531 in Duchenne Muscular Dystrophy (Webinar Recording)
Wave Life Sciences recently joined PPMD for a presentation of interim results from the company’s […]
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DMD treatment WVE-N531 boosts dystrophin: Interim trial data
Treatment with exon 53-skipping therapy WVE-N531 led to significant increases in muscle dystrophin levels along […]
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2024 Rev It Up 5k Raises $27,000 for PPMD
The Rev It Up 5K presented by Mitsubishi Electric Automotive America held their 4th annual […]
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PPMD Hosts Meeting Exploring the Case for Cardiac Transplantation in Duchenne
As part of our ongoing Cardiac Initiative, PPMD is proud to host the upcoming professional […]
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Capricor to seek deramiocel’s FDA approval for DMD heart disease
Capricor Therapeutics will soon begin filing an application seeking U.S. approval of its cell therapy […]
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PPMD Joins Duchenne Parent Project aps Respiratory International Professional Care Meeting
Parent Project Muscular Dystrophy (PPMD) is pleased to announce our participation in the upcoming “Respiratory […]
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MDA Engage offers neuromuscular disease updates, connections
The Muscular Dystrophy Association (MDA) is providing neuromuscular disease (NMD) patients and their families with […]
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Catch Up on Our PPMD Together Event in Seattle, Washington
This past weekend, PPMD convened over 100 attendees at our PPMD Together event in Seattle, […]
