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Focus of NORD study: Rare disease community’s lived experiences
The National Organization for Rare Disorders (NORD) is seeking participants for its survey-based study Living Rare, […]
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My disease progression feels like barreling down a hill with no brakes
When I was 13 and my brother, Tim, was 16, we got skis for Christmas. […]
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Five Tips to Increase Socialization this Spring
Increasing socialization, cultivating meaningful relationships and friendships, and limiting isolation or loneliness in an increasingly […]
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AB-1003 trial for LGMD proceeds after positive recommendation
Asklepios Biopharmaceutical (Askbio) has dosed the first participant in the second group of a Phase […]
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Advocates Unite in Washington D.C. to Champion Duchenne Policy Reforms
PPMD, with a group of more than 150 advocates, heads to Capitol Hill today to […]
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Living with muscular dystrophy, from the perspective of 4 decades
A close friend of 30 years recently asked what my life was like before I […]
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In Case You Missed It…
Quest Media is an innovative adaptive lifestyle platform from MDA. With the power of this […]
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Scientists unlock clues to new treatments for muscular dystrophy
Researchers combined advanced imaging techniques and theoretical physics to observe and explain how nanoclusters of […]
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Quest Podcast: PJ’s Protocol: A Lifesaving Procedure Fueled by Love
In this episode of Quest Podcast, we chat with three pillars of the Duchenne muscular […]
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FDA grants priority review to deramiocel for DMD heart disease
The U.S. Food and Drug Administration (FDA) has accepted Capricor Therapeutics’ application seeking approval of […]
