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Exon-skipping therapy shows promise for DMD44
Delpacibart zotadirsen (del-zota), an investigational exon-skipping therapy from Avidity Biosciences, is demonstrating the potential to
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Exon-skipping therapy shows promise for DMD44
Delpacibart zotadirsen (del-zota), an investigational exon-skipping therapy from Avidity Biosciences, is demonstrating the potential to
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The how and why of living with limb-girdle muscular dystrophy
“He who has a why to live can bear almost any how.” — Friedrich Nietzsche I
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Employer Matching Programs Double the Impact
Anybody who has made a monetary donation to support MDA’s mission knows well that their
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Agamree : un premier traitement approuvé au Canada pour la DMD
Le 25 septembre 2025, Santé Canada a franchi une étape historique en approuvant AGAMREE® (vamorolone)
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Just another Monday: Watch movie, do laundry, throw out my back
Mondays are one of my favorite days of the week as a busy mom to
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CureDuchenne Cares Webinar: Optimizing Cardiac Outcomes in Duchenne
CureDuchenne and Andreas S. Barth, MD, PhD, FAHA, for a community webinar about Optimizing Cardiac
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Motor function linked to weight, height changes in boys with DMD
For boys who start corticosteroids to treat Duchenne muscular dystrophy (DMD), being taller is linked
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MDA Ambassador Guest Blog: Entrepreneurship, Advocacy, and Innovation: Building a More Accessible Future from the Inside Out
Owen Kent is the co-founder and Chief Marketing Officer of Assistive Technology Development (ATDev), a
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MDA Ambassador Guest Blog: Helpful Tips for Accessible Halloween Costumes
Megan Jennings, known professionally as Sybil Thorn, is an artist and freelance creator. Born with
