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Clinical Research Alert: Natural History Study of Individuals with Cardiomyopathy Associated with FRDA
Researchers at Lexeo Therapeutics are seeking individuals with cardiomyopathy associated with Friedreich’s Ataxia (FRDA) to participate
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Letters from Lily: Advice for Parents of Children with Neuromuscular Disease
Hello! For those of you who don’t already know me, my name is Lily and
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Does DMD start in the womb? New research challenges old beliefs.
New findings from research in mice are challenging longstanding beliefs about the causes of Duchenne muscular
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Closing Out the Year with Connection & Community at PPMD Together
Recently, the Duchenne and Becker community gathered virtually for the final PPMD Together meeting of
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Avidity’s New Access Program Marks a Milestone for the Duchenne Community
In 2018, CureDuchenne was the only Duchenne-focused organization to invest in Avidity Biosciences, recognizing the potential of their
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Finding meaning at 30 through my disease communities
Recently, my role at Shalom Medcare shifted from marketing communications assistant to brand executive. This
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Avidity Biosciences Announces U.S. Managed Access Program for del-zota
Avidity Biosciences, Inc. has announced its Managed Access Program (MAP) for delpacibart zotadirsen (del-zota) for
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Avidity announces a Managed Access Program for del-zota, for eligible individuals with Duchenne amenable to skipping exon 44
As an early funder of Avidity Biosciences, CureDuchenne is so happy to share that Avidity
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Clinical Research Alert: Real World Study of Male Fertility Following Risdiplam Treatment
Researchers at Genentech Inc. are seeking adult males treated with risdiplam (Evrysdi) for spinal muscular atrophy
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Quick Guide: Understanding Programs and Benefits for People with Disabilities
Along with the daily challenges of living with a disability, many individuals face the added
