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Early data for experimental DM1 therapy SRP-1003 coming soon
Preliminary data are expected this year for a Phase 1/2 clinical trial testing the investigational […]
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Community Members Reflect on MDA’s Impact
From our earliest days, MDA’s mission has been centered on ensuring that individuals and families […]
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MDA Community Programs Support and Empower
For 75 years, MDA has been dedicated to standing by your side, offering hope, connection, […]
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Progress Now: Research News and Updates Across MDA Diseases Quest Magazine Issue 3, 2025
New approvals New Treatment Approved for gMG In April, the US Food and Drug Administration […]
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Neuromuscular Disease Research: Going Strong
Is hope foolish? For 75 years, MDA has been answering with a resounding, “No.” When […]
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MDA Summer Camp Magic
In 1955, MDA held its first Summer Camp in Sussex, New Jersey. Sixteen campers from […]
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Expanding Leadership, Accelerating Progress
Dear PPMD Community, For more than thirty years, I have had the honor of standing […]
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Elite Para-Dressage Athlete is Ready to Ride to Victory
Para-dressage athlete, Riley Garrett Riley Garrett has found her passion and purpose as a para-dressage […]
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Turkish company to sell Duchenne MD steroid therapy Agamree
The steroid therapy Agamree (vamorolone), which is used for helping to preserve muscle function in […]
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Make Your Voice Heard: Support Adding Duchenne to the RUSP
Every year, thousands of newborns in the U.S. are screened for serious conditions whose early […]
