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Even simple questions become complicated with FSHD
Last night, my wife, Wendy, asked me if I’d like to go out to eat. […]
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CureDuchenne Hosts “Champions in Miami” Event on March 9 to Help Find a Cure for Duchenne Muscular Dystrophy
DJ Irie of the Miami Heat Headlines as Event Brings Together Miami’s Top Business Leaders, […]
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Edgewise Therapeutics’ EDG-5506 on FDA fast track for Duchenne MD
EDG-5506, an oral treatment being developed by Edgewise Therapeutics, has been granted fast track designation […]
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WATCH: PTC Therapeutics — EMFLAZA® Landscape in 2024 (Webinar Recording)
PPMD was recently joined by the team at PTC Therapeutics to discuss upcoming changes and […]
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Cognitive abilities stable over time in Becker MD boys, study finds
Cognitive function in boys with Becker muscular dystrophy (BMD) appear to be stable over time, […]
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PPMD Provides $500,000 in Funding to Kinea Bio Through PPMD Venture Pathways Program to Support Next-Gen Midi-Dystrophin Gene Therapy Development
PPMD is excited to announce that the organization has provided $500,000 in funding to Kinea […]
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MDA advocacy program awards $140K to 7 rare disease groups
With projects spanning gene therapy research, patient advocacy, and air travel safety, seven U.S. organizations […]
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When I get overwhelmed by life as a caregiver, I count my joys
Pulling into a parking spot at my oldest son’s high school, I hit a parked […]
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Finding the Right One: Advice from Experts on Dating with a Disability
“So, are you dating anyone?” Could there possibly be five more scary words spoken to […]
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Update From PPMD’s 2024 PPMD Duchenne Healthcare Professionals Summit
PPMD recently hosted our fifth in-person Duchenne Healthcare Professionals Summit in Sanibel, FL. Over the […]
