-
PPMD’s 30th Annual Conference Session Recordings
Thank you to everyone who helped us celebrate three decades of progress, community, and resilience
-
Expanding Duchenne Clinical Trial Criteria: A Crucial Step Forward
READ THE FULL PRESS RELEASE HERE Introduction The journey towards finding effective treatments for Duchenne
-
Breakthrough in skeletal muscle regeneration
In a finding that opens the door to the development of targeted therapies for various
-
How a son’s MRI stirred up fields of dreams and hopes
This week, one of my boys had to get an MRI. Three of my four
-
CureDuchenne Celebrates FDA’s Launch of Rare Disease Innovation Hub
We at CureDuchenne are excited to acknowledge the recent announcement by the United States Food
-
New gene therapy for muscular dystrophy offers hope
A new gene therapy treatment for Duchenne muscular dystrophy (DMD) shows promise of not only
-
DMD treatment SAT-3247 moves toward 1st trial
Satellos Bioscience is gearing up to launch a Phase 1 clinical trial of its Duchenne
-
My body clock ticks louder because of my Duchenne MD
Nearly two years ago, I authored a column for this website about my reflections on
-
Support World Duchenne Day 2024 with CureDuchenne
As World Duchenne Day (WDD) approaches on September 7, 2024, we at CureDuchenne invite you
-
First oculopharyngeal MD patient sees better swallowing with BB-301
Treatment with the gene therapy BB-301 led to improved swallowing for the first person with
