-
Living with Duchenne grants me unique insight into accessible design
For most of my life, Duchenne muscular dystrophy has defined how I navigate the world.
-
How to find a Duchenne specialist and certified care center
Riketa Smith, a certified medical assistant, shares resources families can use to identify Duchenne specialists
-
Advocating for your child at Duchenne doctor visits
Sheryl Marrazzo shares advice for fellow caregivers on preparing for medical appointments, advocating with facts,
-
MDA 2026: Dyne therapy boosts strength, cognition in DM1
Myotonic dystrophy type 1 (DM1) patients in a Phase 1/2 clinical trial saw gains in
-
Sarepta Announces Initiation of Screening and Enrollment for ENDEAVOR Cohort 8 in Non-Ambulatory Individuals Living with Duchenne
Sarepta Therapeutics, Inc. has announced screening and enrollment are underway in Cohort 8 of the
-
MDA 2026: Duvyzat shows DMD benefits even at lower dose levels
Treatment with Duvyzat (givinostat) was associated with functional gains in boys with Duchenne muscular dystrophy (DMD)
-
Sarepta trial enrolling for ELEVIDYS treatment with enhanced immunosuppression in non-ambulant individuals
Sarepta therapeutics is seeking to enroll 25 non-ambulant individuals with Duchenne in a clinical trial
-
MDA Ambassador Guest Blog: Navigating a Busy Life with a Feeding Tube
Richard Farrell Jr. is 19 years old and lives in Pennsylvania. He was diagnosed with
-
MDA 2026: SGT-003 gene therapy shows early promise for DMD in trial
SGT-003, an investigational gene therapy for Duchenne muscular dystrophy (DMD), worked as expected to increase levels
-
Finding time for some quiet thoughts amid the travel and doctor visits
I’m one of those people who can get lost deep in thought. As a busy
