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This Year, I Am Grateful For Our Journey Together
As I prepare for another holiday to begin, I am again overwhelmed with gratitude for […]
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A walker should help prevent falls, right?
I’m getting more comfortable using my walker. However, it just doesn’t pay to trust the […]
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Equitable Access in Clinical Trials—A Call for Action and Collaboration
Living with Duchenne and Becker presents unique challenges, especially for families from underserved or marginalized […]
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DMD gene therapy GNT0004 set to enter Phase 3 trial in Europe, US
GNT0004, an experimental gene therapy for Duchenne muscular dystrophy (DMD), appears to be working as […]
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Taking control when living with limb-girdle muscular dystrophy
The power to influence or even direct people’s behavior or the course of events is […]
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Changes this year helped me learn my limitations as a caregiver
Life feels busy, which is no surprise to me. My husband, Jason, and I share […]
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Regenxbio starts pivotal trial testing DMD gene therapy RGX-202
Regenxbio has initiated the pivotal phase of a clinical trial testing its experimental gene therapy […]
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How I experienced inclusion (and didn’t) during my education
On Saturday, I presented at the Participation — Inclusion in Action Conference 2024, which was […]
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WATCH: RGX-202 – AFFINITY DUCHENNE Pivotal Program and Functional Data (Webinar Recording)
REGENXBIO recently joined PPMD for a community webinar to provide an update on its AFFINITY […]
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PPMD Culminates 30th Anniversary with Celebratory “Investing in Every Future” Event
PPMD commemorated its 30th anniversary with the “Investing in Every Future” celebratory event on November […]
