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Wave Life Sciences Announces Positive Data from FORWARD-53 Clinical Trial
Wave Life Sciences has announced encouraging interim results from its Phase 2 FORWARD-53 clinical trial […]
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A virtual art show gave FSHDers a chance to show off our talents
I was tempted to do a play on the show “America’s Got Talent” and title […]
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Target to repair injured muscles discovered
A team has discovered a possible therapeutic approach to repair injured muscles either from aging […]
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MDA 2025: Donavon Decker honored for decades of advocacy
Patient advocate Donavon Decker has been given the 2025 MDA Legacy Award for Community Impact […]
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REGENXBIO Shares Positive Biomarker Data from AFFINITY DUCHENNE Trial of RGX-202 Gene Therapy
REGENXBIO Inc. has reported new, positive interim data from two additional patients in the Phase […]
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Mine has been a life of music and joy — and gazing at the stars
Each of my writings in this column has focused on living life with limb-girdle muscular […]
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MDA 2025: DYNE-101 improves finger function in DM1 clinical trial
Treatment with DYNE-101 is leading to improvements in muscle function — with notable gains in […]
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Essential Gear for Traveling with a Disability
Travel should be exciting, not stressful. However, when you have a disability, packing the right […]
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Restoring heart function in Myotonic Dystrophy Type 1
Researchers focused on Myotonic Dystrophy 1 heart problems are testing a novel approach to restore […]
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My 3-year-old is realizing her older brothers with DMD are different
“Mommy, hold me. Mommy, hold me.” These were the words I heard repeatedly from my […]
