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One Family’s Decades of Dedication to MDA Summer Camp
Craig Helget and his brother, Terry Helget, at MDA Summer Camp in 1985. The Helget […]
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Recap: PPMD Together: Minneapolis, MN
This past weekend, PPMD was joined by families, individuals with Duchenne and Becker, clinicians, researchers, […]
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Quest Podcast: Finding Joy in the Midst of Change
In this Quest Podcast episode, we chat with MDA Ambassador Jess Westman about embracing individuality […]
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Watch: Avidity Biosciences – Topline Data from EXPLORE44® Clinical Trial (Webinar Recording)
Avidity Biosciences recently joined PPMD for a community webinar to share topline data from their […]
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MDA 2025: Benefits seen for 3 OPMD patients given gene therapy
The use of experimental gene therapy BB-301 led to improvements in swallowing ability for the […]
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Simply Stated: Updates in Neuromuscular Junction (NMJ) Disorders
The neuromuscular junction (NMJ) disorders are a group of conditions that disrupt the communication between motor […]
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Clinical Research Opportunity: LION-CS101 a Phase 1/2 Study of AB-1003 in Adults with LGMD2I/R9
Researchers at AskBio are seeking adults with genetically confirmed limb-girdle muscular dystrophy (LGMD) type 2I/R9 to […]
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Dr. Peter Marks Resigns from FDA Center for Biologics Evaluation and Research
PPMD is deeply disappointed that Dr. Peter Marks has made the decision to leave his […]
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Pro Tips to Add More Movement to Your Day
Adding more movement or physical activity to each day is a common goal among people […]
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MDA 2025: Duvyzat delays walking loss, lessens lung function decline
Long-term treatment with Duvyzat (givinostat) may help delay the loss of walking ability and lessen […]
