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Regenxbio Webinar
RGX-202: Investigational Gene Therapy for Duchenne Muscular Dystrophy Pivotal Data Update from the AFFINITY DUCHENNE®
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Servier’s Acquisition of Edgewise’s Sevasemten Marks Major Milestone for Becker and Duchenne Muscular Dystrophy Communities
The neuromuscular disease community received encouraging news this week as Edgewise Therapeutics announced the sale of
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MDA Joins Forces to Protect NIH Funding
It’s no secret that MDA advocates are a force on Capitol Hill and have routinely
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Simply Stated: Introduction to Morimoto-Ryu-Malicdan Neuromuscular Syndrome (RFC4 deficiency)
Morimoto–Ryu–Malicdan neuromuscular syndrome (MRMNS) is an inherited condition that was first reported on in late
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Helping my sons with DMD make connections has also helped me
Here are some facts about me: I am an introvert, I am quiet, and my
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Clinical Research Alert: Clinical Study for Adults with Generalized Myasthenia Gravis (gMG)
Researchers at Vor Bio are conducting a global phase 3 clinical study (UPSTREAM MG) for
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FDA to decide on potential first therapy for LGMD2i by late November
No treatments are currently approved and available for limb-girdle muscular dystrophy type 2i (LGMD2i) in
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A Look Back at the First Quest Product Guide of 2026
The MDA Quest Media Product Guide is designed to help you find the products you
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Despite self-image issues, I’m trying to treat my FSHD body as a friend
During a recent facioscapulohumeral muscular dystrophy (FSHD) wellness group meeting via Zoom, a friend of
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Guide to Navigating IEPs and 504 Plans for Kids with Neuromuscular Diseases
As someone living with spinal muscular atrophy (SMA), I know how important it is for
