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AMO Pharma to start AMO-02 Phase 3 trial in adult-onset DM1
AMO Pharma has announced it will conduct a Phase 3 trial of AMO-02 (tideglusib), its
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PPMD Hosts 2024 Cardiac Workshop, May 9-10
PPMD is excited to bring together experts in the cardiac field, spanning clinicians and researchers,
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Paying tribute to the allied healthcare professionals in my life
Last Saturday, I attended a focus group on behalf of a local patient advocacy community
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REGENXBIO Reports First Quarter 2024 Update On Duchenne muscular dystrophy Program
REGENXBIO provided a clinical and regulatory update on their Duchenne muscular dystrophy program highlighting progress
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Update on Pfizer’s Phase 2 Gene Therapy Trial for Duchenne
We are devastated to learn of the tragic loss of a young boy that was
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Global Nonprofit CureDuchenne to Host FUTURES National Conference for the Duchenne and Becker Muscular Dystrophy Community on May 23-26 in Orlando, FL
Four-Day Conference Will Feature Key Opinion Leaders and Notable Speakers including Peter Marks, M.D., Ph.D.,
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WATCH: Community Progress in Duchenne Newborn Screening (Webinar Recording)
PPMD, in collaboration with the Muscular Dystrophy Association (MDA), the EveryLife Foundation for Rare Diseases,
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Baby Duchenne research network receives $250K from PPMD
A $250,000 award from the Parent Project Muscular Dystrophy (PPMD) will support the establishment of
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Rolling Through the Magic: Exploring Disneyland in a Power Wheelchair
Disney Parks can be great places for someone with a power wheelchair to enjoy the
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I’m thankful our doctor can have telehealth sessions with us
Spring is by far the busiest season for my family. I have seven children who
