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BBP-418 improves walking ability in LGMD2i patients in Phase 3 trial
Use of the oral therapy BBP-418 appeared to improve walking ability and lung function in […]
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What to Know About Changes to Food Assistance through SNAP
Funding for the Supplemental Nutrition Assistance Program, which provides food assistance to more than 42 […]
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Avidity Biosciences to be Acquired by Novartis
Yesterday, Avidity Biosciences announced a definitive agreement to be acquired by Novartis. The transaction includes […]
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Avidity Biosciences to be acquired by Novartis
When CureDuchenne invested in Avidity Biosciences in 2018, it was with strong belief in their […]
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I’m giving everything I have for Duchenne MD — in my own way
We are on the brink of November, and it’s beginning to turn cold here in […]
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Letter from Italfarmaco about patient deaths while taking givinostat
Italfarmaco issues a letter to address the recent online discussions about the individuals who have […]
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Italfarmaco Addresses Patient Deaths, DUVYZAT Safety Profile in Community Letter
Italfarmaco, the company that developed DUVYZAT® (givinostat), has shared a letter to the Duchenne muscular […]
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DMD treatment Agamree may avoid issues of traditional steroids
Data from two clinical trials confirm that Agamree (vamorolone), an approved anti-inflammatory treatment for people […]
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This month, I’m celebrating my birthday and disability inclusion
This Saturday, I turn 30. My birthday lands on the same day that many of […]
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Becker Muscular Dystrophy Series Part 1: Neuromuscular Care and Genetics
The first session in PPMD’s Becker muscular dystrophy webinar series brought together clinical experts and […]
