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I ‘muscle through’ LGMD challenges with a little bit of humor
I’ve always had a robust sense of humor. Some people have told me that I’m […]
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Newly Published Study Evaluates Patients’ and Caregivers’ Acceptable Risk from Gene Therapy
A new threshold study, “Re-evaluating Acceptable Risk of Death from Gene Therapy,” has been published […]
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MDA Ambassador Guest Blog: Why I am Speaking Up for Our Community at MDA Hill Day
Faith is 14 years old and lives in Texas. She is a freshman in high […]
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Duchenne MD therapy brogidirsen shows long-term benefit in boys
Brogidirsen (NS-089/NCNP-02), NS Pharma’s investigational therapy for people with Duchenne muscular dystrophy (DMD) who are […]
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Appreciating kind gestures as my health needs increase
In the past couple months, I’ve had more medical challenges than usual. My right arm […]
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This type of meat supercharges muscle growth after workouts
Scientists discovered that lean pork builds muscle more effectively post-workout than high-fat pork, even with […]
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DMD gene therapy leads to sustained benefits for 3 boys in trial
Three boys with Duchenne muscular dystrophy (DMD) who were given the experimental gene therapy GNT0004 […]
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Avidity Biosciences Announces Positive Pre-BLA Meeting with FDA for del-zota
Avidity Biosciences, Inc. has announced the completion of a positive pre-Biologics License Application (BLA) meeting […]
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My sons with Duchenne are each other’s best friends, and that’s OK
Moms worry about their children. As a mother of seven — Lexi, 24; Max, 19; […]
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Standing Together for Access: Ensuring Duchenne Patients Can Benefit from Approved Therapies
PPMD has always fought to ensure that every individual living with Duchenne has access to […]
