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Fracture Management for Duchenne Muscular Dystrophy: Be Prepared with R.A.R.E
Dealing with a fracture is a frightening experience for anyone, especially someone living with Duchenne
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A recent fall has me wondering: Should I use a walker?
I had an incident about a month ago that I’ve been thinking about ever since.
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Exondys 51 extends survival in DMD, long-term study shows
Up to eight years of Exondys 51 treatment (eteplirsen or AVI-4658) extended survival in Duchenne
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60+ Experts Unite to Author Consensus Statement Championing Duchenne Newborn Screening
Over 60 leading experts in genetics, pediatrics, neurology, and public health advocates have authored a
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Reflecting on the beauty in life with Duchenne muscular dystrophy
I have three sons with Duchenne muscular dystrophy (DMD): Max, 18, Rowen, 15, and Charlie,
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Revolutionizing Duchenne Care: A Year of Milestones at The CureDuchenne Clinic
This past year the CureDuchenne Clinic at the Neurology & Neuromuscular Care Center, led by
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CureDuchenne Webinar with italfarmaco | Community Update with ITF Therapeutics: Introducing DUVYZAT™ (givinostat)
Please join us for a session with ITF Therapeutics. Meet members of the ITF Therapeutics
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Gene therapy SGT-003 wins FDA’s rare pediatric disease designation
The U.S. Food and Drug Administration (FDA) has granted rare pediatric disease status to SGT-003,
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Rollout expected by fall in US for new DMD therapy Duvyzat
ITF Therapeutics — which will be responsible for marketing Duvyzat (givinostat), Italfarmaco’s newly approved Duchenne muscular
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When life with Duchenne is hard, I remember the value of friendship
During the month of March, I took a break from writing my column because I
