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FDA approves oral givinostat, as Duvyzat, to treat Duchenne MD
The U.S. Food and Drug Administration (FDA) has approved Italfarmaco’s givinostat, which will now be […]
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ITF Therapeutics Shares Update on DUVYZAT™ Following FDA Approval
Following the FDA’s approval of DUVYZAT (givinostat) on March 21, 2024, ITF Therapeutics, LLC, the […]
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These College Scholarships are Open to People with Disabilities
Going to college can be a life changing experience – from meeting new friends to […]
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PPMD’s 2024 Advocacy Conference Brings Together Community to Support Progress in Fighting for Every Future
Earlier this month, more than 120 PPMD advocates – people with Duchenne and Becker, parents, […]
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WATCH: Sarepta Therapeutics – Data update from MOMENTUM study, SRP-5051 (Webinar Recording)
Sarepta Therapeutics recently joined PPMD for a community webinar: Data Update From the MOMENTUM Study […]
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PTC Therapeutics Announces Plans to Resubmit Translarna™ NDA to FDA
PTC Therapeutics, Inc. has announced that based on recent feedback from the FDA, the company […]
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Agamree, next-gen steroid, now available for DMD patients in US
Agamree (vamorolone) is now available for Duchenne muscular dystrophy (DMD) patients, ages 2 and older, […]
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Italfarmaco Shares Updates Ahead of Givinostat PDUFA Date
Italfarmaco S.p.A. has announced that the full results from the pivotal phase 3 EPIDYS clinical […]
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PTC Therapeutics Provides Key Regulatory Updates
PTC Therapeutics announced that, based on recent feedback from the FDA, by mid-year they plan […]
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7 tips for traveling alone with my 3 sons who have Duchenne
I am traveling this week with my three sons who have Duchenne muscular dystrophy (DMD): […]
