-
RAG-18 granted FDA orphan drug status for Duchenne, Becker MD
The U.S. Food and Drug Administration (FDA) has granted orphan drug status to RAG-18, being
-
Making memories on what was likely my last family vacation
My wife, Wendy, and I recently enjoyed a beach vacation in North Carolina with our
-
Elevidys, one year later: ‘It’s no longer just about coping with DMD’
A little over a year ago, neurologist Sarah Wright administered Elevidys (delandistrogene moxeparvovec-rokl) to then
-
Living on campus is new territory for one son with DMD
My past two columns highlighted significant life events: my daughter’s wedding and my return to
-
Duchenne Added to Massachusetts Newborn Screening Panel
PPMD is excited to announce another significant milestone: Massachusetts has officially approved the addition of
-
Champions in Dallas: An Evening of Culinary Delight and Philanthropy to Support CureDuchenne
Dallas’ Finest Will Unite to Advance Innovative Research and Care for Duchenne Muscular Dystrophy Dallas,
-
FDA gives WVE-N531, exon 53 skipping therapy, supportive status
The U.S. Food and Drug Administration (FDA) has given WVE-N531, an investigational therapy for Duchenne
-
For Duchenne survivors, dealing with grief provides us strength
Earlier this month, I attended the debut of Stephanie Esther Fam’s play “Absence” at Singapore’s
-
WATCH: Advancing DYNE-251 – An Investigational Medicine for Duchenne to Deliver for Patients (Webinar Recording)
Dyne Therapeutics recently joined PPMD for a presentation of clinical data from the DELIVER Trial
-
CureDuchenne Expands Global Initiatives and Spreads Awareness for World Duchenne Day 2024
International-Outreach-and-World-Duchenne-Day-2024-FINALDownload Newport Beach, CA – August 15, 2024 — CureDuchenne, a global leader in research,
