-
PPMD Convenes GI, GU, and Swallowing Experts for Two-Day Workshop
Earlier this month, PPMD convened experts from across the country in Columbus, Ohio for a
-
Percheron Announces Termination of Phase 2B Study of Avicursen for Duchenne
PPMD is disappointed to learn of Percheron Therapeutics’ recent decision to terminate the company’s ongoing
-
There’s never a dull moment living with Duchenne muscular dystrophy
Living with Duchenne muscular dystrophy (DMD) has involved a series of challenges and triumphs, each
-
PepGen Announces Clinical Hold in the U.S. on IND Application to Initiate CONNECT2-EDO51 Phase 2 Study of PGN-EDO51
PPMD is disappointed to learn that PepGen Inc. has received a full clinical hold notice
-
PepGen’s DMD Exon 51 Skipping Program On Clinical Hold In US
PepGen has received a clinical hold notice from the FDA regarding its Investigational New Drug
-
Edgewise Therapeutics Announces Positive Topline Results from CANYON Phase 2 Trial of Sevasemten in Individuals with Becker
Edgewise Therapeutics, Inc., has announced positive topline results from the double-blind, randomized, placebo-controlled Phase 2
-
Edgewise announces Topline results for Becker Phase 2 Trial
As an early funder of Edgewise, CureDuchenne is pleased to share that the Phase 2
-
Sevasemten lowers markers of muscle damage in BMD: Trial
The investigational oral therapy sevasemten significantly reduced markers of muscle damage in people with Becker
-
New drug shows promise against Duchenne muscular dystrophy
A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder
-
How my teaching job reminds me that I’m more than a caregiver
I’m more than a caregiver, but it took a recent life change for me to
