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Duchenne Added to Massachusetts Newborn Screening Panel
PPMD is excited to announce another significant milestone: Massachusetts has officially approved the addition of […]
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Champions in Dallas: An Evening of Culinary Delight and Philanthropy to Support CureDuchenne
Dallas’ Finest Will Unite to Advance Innovative Research and Care for Duchenne Muscular Dystrophy Dallas, […]
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FDA gives WVE-N531, exon 53 skipping therapy, supportive status
The U.S. Food and Drug Administration (FDA) has given WVE-N531, an investigational therapy for Duchenne […]
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For Duchenne survivors, dealing with grief provides us strength
Earlier this month, I attended the debut of Stephanie Esther Fam’s play “Absence” at Singapore’s […]
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WATCH: Advancing DYNE-251 – An Investigational Medicine for Duchenne to Deliver for Patients (Webinar Recording)
Dyne Therapeutics recently joined PPMD for a presentation of clinical data from the DELIVER Trial […]
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CureDuchenne Expands Global Initiatives and Spreads Awareness for World Duchenne Day 2024
International-Outreach-and-World-Duchenne-Day-2024-FINALDownload Newport Beach, CA – August 15, 2024 — CureDuchenne, a global leader in research, […]
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Confronting the financial burdens of DMD with a heap of faith
I have seven children, and three of them are living with Duchenne muscular dystrophy (DMD): […]
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Why having my own ‘escape hatch’ is key to my happiness
Roughly four decades into living with limb-girdle muscular dystrophy, I’ve developed numerous ways to thrive. […]
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Del-zota increases dystrophin in DMD patients, new trial data show
Avidity Biosciences‘ delpacibart zotadirsen, or del-zota for short — formerly called AOC 1044 — was […]
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Ladies Luncheon Newport Beach to Debut at Shady Canyon Golf Club on October 15 Benefiting CureDuchenne Inaugural Event Features Fashion, Food, and Fun to Raise Funds for Cutting-Edge Duchenne Muscular Dystrophy Research
NEWPORT BEACH, California (August 13, 2024) – CureDuchenne, a global nonprofit dedicated to funding and […]
