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Share your NOW: The impact of up-to-date data in The Duchenne Registry
The Duchenne Registry is designed as a longitudinal (long-term) research study, collecting information from the
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Fire Fighters Go the Distance for MDA
Thomas Beers knew from a very young age that he wanted to be a fire
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Now measuring my life in pounds, ounces, minutes, and seconds
In a recent column, I talked about paring down my music rig and retiring my
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MDA Ambassador Guest Blog: What I’ve Learned as a Disability and Wellbeing Researcher
Payton Rule is a Clinical Psychology PhD student at Washington University in St. Louis, where
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Myotonic dystrophy patients in US face higher healthcare costs: Study
People with myotonic dystrophy (DM) use more healthcare resources and face higher associated costs than
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Duvyzat recommended for EU approval as DMD treatment
The Committee for Medicinal Products for Human Use, an arm of the European Medicines Agency
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Watch: Sarepta Therapeutics – Duchenne Gene Therapy Update (Webinar Recording)
Sarepta Therapeutics recently joined PPMD for a community webinar to share the latest updates on
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The BELS Questionnaire: A New Tool to Support Your Child’s Emotional Wellbeing
PPMD is excited to share that a new tool, the BELS (Behavioral, Emotional, Learning, and
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Simply Stated: Updates in Amyotrophic Lateral Sclerosis (ALS)
Amyotrophic lateral sclerosis (ALS) is a rare, progressive neurodegenerative disease that leads to muscle weakness,
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MDA Ambassador Guest Blog: How the Power of a Few People (and a Dog) Can Change Your World
David Daw is 56 years old and lives in Kingston New York with his wife
