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Satellos Announces Positive Functional Data from Phase 1b Open-Label Trial of SAT-3247 in Adults with Duchenne
Satellos Bioscience Inc. has announced encouraging data from the company’s Phase 1b open-label study of […]
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How to Manage Stress and Fear in Uncertain Times
People in the neuromuscular disease community are hearing many different reports about policy and funding […]
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Investigational gene therapy shows benefits in two boys with DMD
An investigational gene therapy called GNT0004 has demonstrated sustained stabilization of motor function at up to […]
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Florida Signs Duchenne Newborn Screening into Law
We are delighted to share exciting news for the Duchenne community: Governor Ron DeSantis has […]
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MDA Conference Grants Support Resources to the Community
The Muscular Dystrophy Association (MDA) provides a significant number of research grants each year to […]
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How my fight for inclusive access to a soccer stadium paid off
As a Duchenne muscular dystrophy survivor, I’ve spent much of my life on the outside […]
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NHL All-Star Troy Terry and Wife Dani to Host CureDuchenne Golf Shootout on September 12–13, Continuing a Legacy of Impact for Duchenne Muscular Dystrophy
Event Has Raised Over $6.3 Million to Date, Advancing Lifesaving Research and Therapies for Individuals […]
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Analyses show benefits of DMD gene therapy Elevidys
The one-time gene therapy Elevidys (delandistrogene moxeparvovec-rokl) was associated with stabilizations in motor function for […]
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Life with Lily #2: Advocating for Disability Rights
Advocacy doesn’t always look bold or dramatic. Most of the time, it’s quiet, messy, and […]
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Understanding the Threats to the ACL – and What It Means for You
In late March, the U.S. Department of Health and Human Services (HHS) announced a ‘dramatic […]
