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CureDuchenne Fuerza 2025 Unites Mexico and Global Duchenne Community in Landmark Event
CureDuchenne Fuerza 2025, hosted by the CureDuchenne International Program on October 25, 2025, brought together more than 400 attendees
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We shout, ‘Not today, Duchenne!’ and Duchenne whispers back
My oldest son, Max, was diagnosed with Duchenne muscular dystrophy (DMD) in 2010, when he
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Welcoming the New Members of PAAC for Fall 2025
PPMD’s Adult Advisory Committee (PAAC) recently expanded with 19 inspiring new members, bringing the committee
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Exoskeletons Improve Movement for Those with Neuromuscular Diseases
Exoskeletons are wearable devices that can provide physical support and improve functional mobility for people
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DMD drugs show promise despite trial’s missing main goal: Sarepta
Exon-skipping therapies Amondys 45 (casimersen) and Vyondys 53 (golodirsen) show “positive and encouraging trends” for people
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Updates on Entrada’s exon skipping clinical trials
As an early investor in Entrada Therapeutics, we are pleased to share their progress on
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Advancing Brain and Behavior Care in Dystrophinopathy
Recently, PPMD led a meeting with experts from across the US and Europe to discuss
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Guest Voice: Caregiving isn’t easy, but it’s not a burden
We had only been married a few months when my husband woke me in the
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Finding balance as I manage my DMD-associated cardiomyopathy
Turning 30 last month was a significant milestone in my Duchenne muscular dystrophy (DMD) journey.
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Solid Biosciences Shares Interim Data from INSPIRE DUCHENNE Trial of SGT-003
Solid Biosciences Inc. has announced positive new interim data from the Phase 1/2 INSPIRE DUCHENNE
