-
Simply Stated: Updates in Neuropathy Ataxia and Retinitis Pigmentosa (NARP) Syndrome
Neuropathy ataxia and retinitis pigmentosa (NARP) syndrome is a rare, maternally-inherited condition caused by mutations
-
My family caregivers are feeling the pressure
I have a growing list of limitations, as a result of my facioscapulohumeral muscular dystrophy
-
BBP-418 improves walking ability in LGMD2i patients in Phase 3 trial
Use of the oral therapy BBP-418 appeared to improve walking ability and lung function in
-
What to Know About Changes to Food Assistance through SNAP
Funding for the Supplemental Nutrition Assistance Program, which provides food assistance to more than 42
-
Avidity Biosciences to be Acquired by Novartis
Yesterday, Avidity Biosciences announced a definitive agreement to be acquired by Novartis. The transaction includes
-
Avidity Biosciences to be acquired by Novartis
When CureDuchenne invested in Avidity Biosciences in 2018, it was with strong belief in their
-
I’m giving everything I have for Duchenne MD — in my own way
We are on the brink of November, and it’s beginning to turn cold here in
-
Letter from Italfarmaco about patient deaths while taking givinostat
Italfarmaco issues a letter to address the recent online discussions about the individuals who have
-
Italfarmaco Addresses Patient Deaths, DUVYZAT Safety Profile in Community Letter
Italfarmaco, the company that developed DUVYZAT® (givinostat), has shared a letter to the Duchenne muscular
-
DMD treatment Agamree may avoid issues of traditional steroids
Data from two clinical trials confirm that Agamree (vamorolone), an approved anti-inflammatory treatment for people
