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Del-zota for DMD awarded FDA breakthrough therapy designation
The U.S. Food and Drug Administration (FDA) granted breakthrough therapy designation to delpacibart zotadirsen, known […]
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How art can foster connection in the disability community
Last Sunday, my girlfriend, Amanda, and I co-led an art workshop that brought us both […]
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Avidity Biosciences granted Breakthrough Therapy Designation for exon-44 skipping therapeutic, del-zota
CureDuchenne was an early investor in Avidity Biosciences in 2016, and congratulates the company for receiving Breakthrough Therapy […]
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FDA Grants Breakthrough Therapy Designation to Avidity’s del-zota
Avidity Biosciences, Inc. today shared that the U.S. Food and Drug Administration (FDA) has granted […]
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Sarepta voluntarily halts Elevidys shipments in US after FDA request
Sarepta Therapeutics is voluntarily halting all shipments of Elevidys (delandistrogene moxeparvovec-rokl) in the U.S. after a […]
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The importance of advance directives, especially with MD
Amid the hustle and bustle of daily life, many people tend to put off what […]
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Update on ELEVIDYS Shipments in the U.S.
This evening, Sarepta Therapeutics issued a press release stating that it has voluntarily and temporarily […]
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MDA Ambassador Guest Blog: Parenting, LGMD, and Choosing Joy
Chris Carroll is 41 years old and lives with his wife Joy and two children […]
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ELEVIDYS UPDATE
Read Sarepta’s letter to the community Shared July 18, 2025 Duchenne Community Letter 7.18.2025Download The […]
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As I look in the mirror, I’m proud of the person staring back at me
Years ago, I had my colors done: I’m a winter. Dark blues, greens, scarlets, royal […]
