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NEW: Livestream with the PAAC
What can you learn from the PPMD Adult Advisory Committee (PAAC) that you can’t ask Google?
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MDA taps Bridgebio funding to improve LGMD care coordination
Bridgebio is providing $100,000 to the Muscular Dystrophy Association (MDA) to advance projects aimed at
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RegenXBio announces positive topline results from pivotal Phase 3 microdystrophin gene therapy trial
RegenXBio shared positive topline results from their pivotal Phase 3 AFFINITY DUCHENNE study of RGX-202
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REGENXBIO Shares Topline Results from Pivotal Phase III AFFINITY DUCHENNE® Study of RGX-202
REGENXBIO Inc. has announced positive topline and interim functional data from the pivotal Phase III
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GEMMABio Announces Duchenne Muscular Dystrophy Program, Shares Preclinical Data for Investigational Gene Therapy for Duchenne
Today, Gemma Biotherapeutics (GEMMABio), a clinical‑stage, global, genetic therapeutics company, shared information about the company’s
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MDA Ambassador Guest Blog: Embers of Resilience Through Depression
Joshua Vinson enjoys rain, camping, and cooking. Joshua works as a Quality Assurance Specialist in
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When it comes to accessibility, even the best-laid plans can go awry
On May 1, my daughter Jill graduated from the University of Pittsburgh with a master’s
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Clinical Research Alert: Natural History Study in Individuals with Myotonic Dystrophy Type 2
Researchers at the University of Rochester are seeking adults with myotonic dystrophy type 2 (DM2) for
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Exercise in Dystrophinopathy: What Families Need to Know
PPMD recently hosted a webinar centered on common questions from families: is exercise recommended in
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This simple strength test could predict how long you live
Staying strong may be one of the biggest secrets to living longer — especially for
