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Upsher-Smith launches new DMD support websites for Kymbee treatment
Upsher-Smith Laboratories has launched two new websites to support people with Duchenne muscular dystrophy (DMD)
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Clinical Research Alert: Clinical Study for Adults with Late-Onset Pompe Disease (LOPD)
Researchers at Shionogi Inc. are conducting a phase 2 clinical trial for adults with late-onset
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Exploring other mobility devices when a walker is no longer sufficient
Last week was a busy one for me. In addition to my normal activities, I
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Collaboration aims to improve design of FSHD clinical trials
A new collaboration aims to improve the design of clinical trials testing potential treatments for
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Pompe Disease and the Real Story Behind Dr. Stonehill, John Crowley, and ‘Extraordinary Measures’
“Don’t hope for a miracle. Make one,” is the powerful tag line from “Extraordinary Measures,”
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MDA Ambassador Guest Blog: My Pompe Journey
Kathryn Arvidson champions accessible mental health treatment for people with disabilities. Kathryn was diagnosed as
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I won’t apologize for having 3 children with Duchenne MD
I have always been an open book about my life. I am a writer, caregiver,
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FDA clears trial testing Mesoblast cell therapy in kids with DMD
The U.S. Food and Drug Administration (FDA) has given Mesoblast the go-ahead to launch a
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Quest Podcast: From Roadmap to Emmy: Samuel and Dan Habib on Filmmaking, Family, and Disability
In this Quest Podcast episode, we chat with Emmy Award-winning filmmaker and disability advocate Samuel
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In Case You Missed It…
Quest Media is an innovative, adaptive lifestyle platform from MDA. With the power of this
