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MDA Ambassador Blog: Steps of Strength: Finding Hope and Community on Our Duchenne Journey
Katie Brooks is a mom of two incredible little boys, Dominic and Daniel. She was born
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Everything You Need to Know About Clinical Trials for Neuromuscular Diseases
Clinical trials are the cornerstone of research. When a new medical treatment, device, or strategy
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Study finds DMD affects vascular muscles as well as skeletal ones
Duchenne muscular dystrophy (DMD) causes dysfunction of muscle cells that help move blood through the
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Families Are Waiting
A recent 60 Minutes segment examining the cost of gene therapy put a national spotlight
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A Year Built Together: Reflections on 2025 and the Road Ahead
Stepping into this role in such a historic year has been humbling and inspiring. This
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Simply Stated: Understanding Idiopathic Inflammatory Myopathies
The idiopathic inflammatory myopathies (IIMs) are a group of rare autoimmune muscle diseases that include
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Life is so much easier with a sense of humor
I’m feeling funny today — humorous, in fact. Brimming with sarcasm and a splash of
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Watch: Capricor Therapeutics — HOPE-3 Community Update (Webinar Recording)
PPMD recently held a community webinar with Capricor Therapeutics, during which the company shared their
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BREAKING NEWS: U.S. Department of Health and Human Services (HHS) adds Duchenne Muscular Dystrophy to the Recommended Uniform Screening Panel (RUSP) for Newborn Screening
CureDuchenne applauds the U.S. Department of Health and Human Services (HHS) for adding Duchenne muscular dystrophy to
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Dyne Webinar: Positive Topline Results from DELIVER trial in Exon 51 DMD
A presentation with Dr. Doug Kerr, Chief Medical Officer at Dyne Therapeutics. Dr. Kerr shares
