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Turkish company to sell Duchenne MD steroid therapy Agamree
The steroid therapy Agamree (vamorolone), which is used for helping to preserve muscle function in […]
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Make Your Voice Heard: Support Adding Duchenne to the RUSP
Every year, thousands of newborns in the U.S. are screened for serious conditions whose early […]
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REGENXBIO AFFINITY DUCHENNE: Trial of Investigational RGX-202 Gene Therapy
In this webinar, Dr. Naz Dastgir, Executive Medical Director and Clinical Development Lead for RGX-202 […]
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Back to School Resources for Duchenne in 2025
Back to School with Duchenne: Navigating this new 2025 school year is a challenge for […]
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Solid Biosciences Shares Update on INSPIRE DUCHENNE Trial of SGT-003
Solid Biosciences has shared an update on the company’s Phase 1/2 INSPIRE DUCHENNE trial evaluating […]
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Celebrating a long-in-the-works family music songfest
I’m a musician, and so are my brothers, Ron and Tim. We’ve all played professionally, […]
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Calling All Adults with Duchenne & Becker: Join the 2026 PPMD Adult Advisory Committee (PAAC)
Have you been looking for a way to engage with the community more? Do you […]
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Solid Biosciences announced a widely anticipated update on their INSPIRE DUCHENNE Phase 1/2 clinical trial of SGT-003
Solid Biosciences announced a widely anticipated update on their INSPIRE DUCHENNE Phase 1/2 clinical trial […]
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MDA Guest Ambassador: Ten Tips for High School Life with a Disability
Madison is from Baton Rouge, Louisiana, and lives with congenital muscular dystrophy. She is an […]
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Hidden role of MYOD protein may lead to new MD therapies: Study
A protein called MYOD, which is known to control the growth of muscle stem cells […]
