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CureDuchenne Celebrates FDA’s Launch of Rare Disease Innovation Hub
We at CureDuchenne are excited to acknowledge the recent announcement by the United States Food […]
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DMD treatment SAT-3247 moves toward 1st trial
Satellos Bioscience is gearing up to launch a Phase 1 clinical trial of its Duchenne […]
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Support World Duchenne Day 2024 with CureDuchenne
As World Duchenne Day (WDD) approaches on September 7, 2024, we at CureDuchenne invite you […]
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First oculopharyngeal MD patient sees better swallowing with BB-301
Treatment with the gene therapy BB-301 led to improved swallowing for the first person with […]
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My body clock ticks louder because of my Duchenne MD
Nearly two years ago, I authored a column for this website about my reflections on […]
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PPMD Applauds FDA Launch of Rare Disease Innovation Hub — A Milestone for Rare Disease Patients
Parent Project Muscular Dystrophy (PPMD) welcomes the recent announcement by the United States Food and […]
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A Father Rises in Support of His Son
A Father Rises in Support of His Son: On this powerful episode of the “In […]
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Losmapimod improved, stabilized FSHD upper limb function: Study
One year of losmapimod taken twice a day improved or stabilized upper limb function and […]
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Fun summer activities that are still doable with Duchenne
I often read social media posts from moms asking for safe and fun ideas for […]
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NHL All-Star Ryan Getzlaf Returns to the Links for the 13th Annual Getzlaf Golf Shootout on September 13-14, Benefiting CureDuchenne
Event Has Raised More Than $5.8 Million Over the Last 12 Years to Drive a […]
