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International Day of Women and Girls in Science: MDA Spotlight on Elizabeth Madole
International Women and Girls in Science Day, February 11, endeavors to acknowledge and celebrate the invaluable role that women and girls play in accelerating change and discovery in the professional realm of science, technology, engineering, and math (STEM). In recognition of International Day of Women and Girls in Science, the Muscular Dystrophy Association (MDA) is…
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The rule of 10 helps me navigate bad days with LGMD
We all have bad days, but hopefully they are few and far between. Bad days can overwhelm, dampen your spirit, and leave you feeling angry, sad, or depressed. You may need to take a break from whatever has caused them. First, let me clarify that I am talking about bumps in the road, not trauma.…
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In Case You Missed It…
Quest Media is an innovative, adaptive lifestyle platform from MDA. With the power of this platform, we foster awareness and empowerment and have important conversations with experts, thought leaders, and members of the neuromuscular disease community about topics that matter to them and to the larger community of individuals with disabilities. With so many valuable…
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I have 5 essential tools for managing cold and flu season with Duchenne MD
When the germs of cold and flu season find their way into the Vertin household, they crash our party of nine, and no one is spared. A cold or flu can be especially dangerous for my three sons with Duchenne muscular dystrophy (DMD) — Max, Rowen, and Charlie — because they have compromised immune systems…
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Cardiac Care for Female Carriers
While February may be known for Valentine’s Day candy and flowers, it is also American Heart Month! Within the dystrophinopathy community, keeping heart health front and center is especially critical. It is estimated that around 67% of mothers of children with Duchenne muscular dystrophy and nearly 90% of mothers of children with Becker muscular dystrophy…
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Napa in Newport Returns as a Three-Day Celebration of Napa Wine Benefiting CureDuchenne
Napa’s Finest Come to Newport Beach, Led by Vintner Chair Peter Michael Winery NEWPORT BEACH, California (February 5, 2026) – CureDuchenne, a global leader in accelerating research and care for Duchenne muscular dystrophy, has announced that its annual Napa in Newport event will debut as an elevated weekend-long experience, showcasing the best of Napa Valley in coastal luxury. Taking place March…
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CureDuchenne Announces Educational Events for Duchenne and Becker Families and Caregivers
Free nationwide events deliver expert guidance and meaningful connections for families impacted by Duchenne and Becker muscular dystrophy NEWPORT BEACH, Calif., February 4, 2025 – CureDuchenne, a global leader in advancing research and improving patient care for individuals with Duchenne and Becker muscular dystrophy, today announced the 2026 lineup of CureDuchenne CARES events, designed to deliver the latest treatment insights,…
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Our 2026 Advocacy Agenda
After a year of twists and turns in 2025, MDA and its advocates are even more motivated to raise their voices and create change for the neuromuscular community. Check out the roadmap for the next 12 months and learn how you can make an impact in 2026. Celebrating early victories on previous priorities 2026 got…
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FDA fast tracks Dyscorban for treating heart problems in Duchenne
The U.S. Food and Drug Administration (FDA) has granted fast track designation to Dyscorban (ifetroban), Cumberland Pharmaceuticals’ treatment candidate for heart problems in Duchenne muscular dystrophy (DMD). Dyscorban has been tested in the Phase 2 FIGHT DMD trial (NCT03340675), with data showing that it improved heart function and reduced markers of heart damage in individuals with…
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Terapia Génica ELEVIDYS
Terapia Génica ELEVIDYS: Actualización Comunitaria Más Reciente con Sarepta Therapeutics Watch HERE The post Terapia Génica ELEVIDYS appeared first on CureDuchenne.
