-
Clinical Research Alert: Phase 1/2 Study of SGT-003 in Boys with DMD
Researchers at Solid Biosciences are seeking boys with Duchenne muscular dystrophy (DMD) to participate in a phase 1/2 clinical trial (INSPIRE DUCHENNE) to evaluate the safety and efficacy of the investigational gene therapy (SGT-003). DMD is caused by the loss of the dystrophin protein, which is important for the structure and function of muscle cells. SGT-003…
-
Five Common Corticosteroid Questions and Considerations
Corticosteroids are anti-inflammatory drugs that play an important role in treating some neuromuscular diseases. These medications are the fastest and most efficient way to control inflammation, and they can also reduce pain and suppress overactive immune system responses. According to Dr. Elizabeth McNally, a cardiologist and Director of Northwestern University’s Center for Genetic Medicine in…
