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Sarepta voluntarily halts Elevidys shipments in US after FDA request
Sarepta Therapeutics is voluntarily halting all shipments of Elevidys (delandistrogene moxeparvovec-rokl) in the U.S. after a […]
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The importance of advance directives, especially with MD
Amid the hustle and bustle of daily life, many people tend to put off what […]
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Update on ELEVIDYS Shipments in the U.S.
This evening, Sarepta Therapeutics issued a press release stating that it has voluntarily and temporarily […]
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MDA Ambassador Guest Blog: Parenting, LGMD, and Choosing Joy
Chris Carroll is 41 years old and lives with his wife Joy and two children […]
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ELEVIDYS UPDATE
Read Sarepta’s letter to the community Shared July 18, 2025 Duchenne Community Letter 7.18.2025Download The […]
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As I look in the mirror, I’m proud of the person staring back at me
Years ago, I had my colors done: I’m a winter. Dark blues, greens, scarlets, royal […]
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ELEVIDYS Update
PPMD acknowledges the media reports that the U.S. Food and Drug Administration (FDA) will request […]
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Dosing begins in gene therapy trial for DMD-linked heart disease
The first patient has been dosed as part of a Phase 1b clinical trial of […]
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Sarepta Therapeutics Announces Update on ELEVIDYS Label, Company Restructuring
Yesterday afternoon, Sarepta issued a press release and community letter which included updates related to […]
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New preclinical data from Precision BioSciences’s gene editing program for Duchenne
Precision BioSciences is developing a novel gene editing approach for individuals with dystrophin mutations in […]
