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Calling All Adults with Duchenne & Becker: Join the 2025 PPMD Adult Advisory Committee
Have you been looking for a way to engage with the community more? Do you […]
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The missed milestones in the teenage years because of DMD
I have three teenage sons — Max, 18, Rowen, 15, and Charlie, 13 — who […]
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Solid Biosciences Shares Updates on INSPIRE DUCHENNE Clinical Trial of SGT-003
Yesterday, Solid Biosciences shared new updates on the INSPIRE DUCHENNE clinical trial for their next-generation […]
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Patients with certain mutations lose their walking ability earlier: Study
Specific genetic mutations in Duchenne muscular dystrophy (DMD) influence how long patients retain the ability to […]
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REGENXBIO Shares Updates on Phase I/II AFFINITY DUCHENNE® trial of RGX-202
Yesterday, REGENXBIO shared important updates on their Phase I/II AFFINITY DUCHENNE® trial of RGX-202 for […]
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Supporting artists with disabilities through a new business venture
Three weeks ago, my girlfriend, Amanda, and I embarked on a unique journey by co-founding […]
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I always try to pause to appreciate the small victories
I’m currently continuing to do the exercises my physical therapist recommended during my last therapy […]
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Sarepta Announces Discontinuation of SRP-5051 Development for Duchenne
Sarepta Therapeutics today announced that the company is discontinuing its SRP-5051 (vesleteplirsen) development program, including […]
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Phase 1/2 trial of del-brax enrolling new, possibly pivotal FSHD group
A new patient group is being enrolled in a Phase 1/2 trial of delpacibart braxlosiran […]
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WATCH: Exploring Muscle Regeneration – A New Approach with Satellos (Webinar Recording)
Satellos recently joined PPMD for a community webinar exploring a new approach for the treatment […]
