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Every week, we try to organize chaos in our family of 9
What’s a typical week as a caregiver of three sons with Duchenne muscular dystrophy (DMD) […]
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Capricor Initiates Rolling Submission of Biologics License Application (BLA) for Deramiocel (CAP-1002)
Capricor Therapeutics Initiates Rolling Submission of Biologics License Application (BLA) for Deramiocel (CAP-1002) for the […]
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13th Annual Getzlaf Golf Shootout Raises Nearly $500,000 for CureDuchenne, Welcoming Troy and Danielle Terry as New Hosts
Ryan and Paige Getzlaf Pass the Torch to Anaheim Ducks All-Star Troy Terry and His […]
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Protected: 2024 Annual Congress of the World Muscle Society Updates
This content is password protected. To view it please enter your password below: Password: The […]
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Educating all ages about living with muscular dystrophy
In my four decades of life with limb-girdle muscular dystrophy, I’ve become comfortable educating everyone […]
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C-Path to lead new task force seeking to advance LGMD therapies
The Critical Path Institute (C-Path) is launching a task force to advance the development of […]
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This time, new medical equipment is hard for me to accept
Our house is getting a new piece of medical equipment this week. That’s happened before, […]
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Rare pediatric disease designation granted to LAMA2-CMD therapy
The U.S. Food and Drug Administration (FDA) has granted rare pediatric disease designation to MDL-101, […]
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WATCH: Interim Results from FORWARD-53 Study of WVE-N531 in Duchenne Muscular Dystrophy (Webinar Recording)
Wave Life Sciences recently joined PPMD for a presentation of interim results from the company’s […]
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DMD treatment WVE-N531 boosts dystrophin: Interim trial data
Treatment with exon 53-skipping therapy WVE-N531 led to significant increases in muscle dystrophin levels along […]
