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EDGEWISE THERAPEUTICS ANNOUNCES POSITIVE TWO-YEAR TOPLINE RESULTS
Edgewise Therapeutics Announces Positive Two-Year Topline Results from the ARCH Open Label Trial of Sevasemten […]
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PPMD Launches First State-Specific Duchenne Advocacy Day in Illinois
PPMD is proud to announce the launch of our first state-specific Duchenne Advocacy Day in […]
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Duchenne Siblings Study Published: Assessing Early Diagnosis from the Perspective of Parents with Multiple Children Diagnosed with Duchenne
For more than a decade, PPMD has been at the forefront of advocating for Duchenne […]
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Diagnostic testing IDs 2 gene mutations causing LGMD type R1
Diagnostic testing of individuals in India suspected of having limb-girdle muscular dystrophy (LGMD) revealed two […]
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Fracture Management for Duchenne Muscular Dystrophy: Be Prepared with R.A.R.E
Dealing with a fracture is a frightening experience for anyone, especially someone living with Duchenne […]
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A Decade of Distinction: Napa in Newport Celebrates 10 Years of Wine, Culinary Excellence, and Philanthropy
Southern California’s Premier Wine Event Brings Together Acclaimed Napa Valley Vintners Under One Roof to […]
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I’m feeling all the emotions as my oldest son reaches a big milestone
I have three sons with Duchenne muscular dystrophy (DMD): Max, 18, Rowen, 15, and Charlie, […]
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A recent fall has me wondering: Should I use a walker?
I had an incident about a month ago that I’ve been thinking about ever since. […]
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Exondys 51 extends survival in DMD, long-term study shows
Up to eight years of Exondys 51 treatment (eteplirsen or AVI-4658) extended survival in Duchenne […]
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60+ Experts Unite to Author Consensus Statement Championing Duchenne Newborn Screening
Over 60 leading experts in genetics, pediatrics, neurology, and public health advocates have authored a […]
