-
PPMD Announces Pediatric Certified Duchenne Care Center at Penn State Health Children’s Hospital
Today PPMD announced the expansion of our renowned Certified Duchenne Care Center (CDCC) Program with
-
Sarepta Therapeutics Announces U.S. FDA Acceptance of an Efficacy Supplement to Expand the ELEVIDYS Indication
The FDA will make a decision whether or not to grant full approval of Sarepta’s
-
The things we don’t talk about as Duchenne caregivers
When three of my sons were diagnosed with Duchenne muscular dystrophy more than 10 years
-
FDA Accepts Efficacy Supplement to Expand ELEVIDYS Indication
PPMD is excited to learn that the U.S. Food and Drug Administration (FDA) has accepted
-
How to Identify and Manage Fat Embolism Syndrome (FES) in Fractures
Fat embolism syndrome (FES) is a potentially life-threatening condition that can be triggered by bone
-
Even simple questions become complicated with FSHD
Last night, my wife, Wendy, asked me if I’d like to go out to eat.
-
CureDuchenne Hosts “Champions in Miami” Event on March 9 to Help Find a Cure for Duchenne Muscular Dystrophy
DJ Irie of the Miami Heat Headlines as Event Brings Together Miami’s Top Business Leaders,
-
Edgewise Therapeutics’ EDG-5506 on FDA fast track for Duchenne MD
EDG-5506, an oral treatment being developed by Edgewise Therapeutics, has been granted fast track designation
-
Cognitive abilities stable over time in Becker MD boys, study finds
Cognitive function in boys with Becker muscular dystrophy (BMD) appear to be stable over time,
-
WATCH: PTC Therapeutics — EMFLAZA® Landscape in 2024 (Webinar Recording)
PPMD was recently joined by the team at PTC Therapeutics to discuss upcoming changes and
