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PPMD Announces Pediatric Certified Duchenne Care Center at Penn State Health Children’s Hospital
Today PPMD announced the expansion of our renowned Certified Duchenne Care Center (CDCC) Program with […]
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Sarepta Therapeutics Announces U.S. FDA Acceptance of an Efficacy Supplement to Expand the ELEVIDYS Indication
The FDA will make a decision whether or not to grant full approval of Sarepta’s […]
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The things we don’t talk about as Duchenne caregivers
When three of my sons were diagnosed with Duchenne muscular dystrophy more than 10 years […]
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FDA Accepts Efficacy Supplement to Expand ELEVIDYS Indication
PPMD is excited to learn that the U.S. Food and Drug Administration (FDA) has accepted […]
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How to Identify and Manage Fat Embolism Syndrome (FES) in Fractures
Fat embolism syndrome (FES) is a potentially life-threatening condition that can be triggered by bone […]
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Even simple questions become complicated with FSHD
Last night, my wife, Wendy, asked me if I’d like to go out to eat. […]
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CureDuchenne Hosts “Champions in Miami” Event on March 9 to Help Find a Cure for Duchenne Muscular Dystrophy
DJ Irie of the Miami Heat Headlines as Event Brings Together Miami’s Top Business Leaders, […]
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Edgewise Therapeutics’ EDG-5506 on FDA fast track for Duchenne MD
EDG-5506, an oral treatment being developed by Edgewise Therapeutics, has been granted fast track designation […]
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Cognitive abilities stable over time in Becker MD boys, study finds
Cognitive function in boys with Becker muscular dystrophy (BMD) appear to be stable over time, […]
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WATCH: PTC Therapeutics — EMFLAZA® Landscape in 2024 (Webinar Recording)
PPMD was recently joined by the team at PTC Therapeutics to discuss upcoming changes and […]
