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Caregiving for sons with DMD is like being a frog in boiling water
One of my favorite early-summer memories is from when my sons Max and Rowen were […]
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Next-gen gene therapy SGT-003 named FDA orphan drug
SGT-003, a next-generation gene therapy candidate for Duchenne muscular dystrophy (DMD) being developed by Solid Biosciences, […]
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Astellas Releases Results of Discontinued Phase 1b Study of ASP0367
Astellas has shared results of the Phase 1b study of ASP0367 (MA-0211), an oral investigational drug. The […]
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PPMD Hosts 2024 Duchenne Healthcare Professionals Summit
Each January, PPMD brings together experts in the field for our Duchenne Healthcare Professionals Summit […]
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Turning Challenges into Opportunities: A Conversation With Justin Skeesuck From “I’ll Push You”
Justin Skeesuck, a 48-year-old Idahoan featured in the documentary “I’ll Push You,” started losing the […]
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